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Clinical trials for 2019-003781-41

The European Union Clinical Trials Register   allows you to search for protocol and results information on:
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    The EU Clinical Trials Register currently displays   44416   clinical trials with a EudraCT protocol, of which   7423   are clinical trials conducted with subjects less than 18 years old.   The register also displays information on   18700   older paediatric trials (in scope of Article 45 of the Paediatric Regulation (EC) No 1901/2006).

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    1 result(s) found for: 2019-003781-41. Displaying page 1 of 1.
    EudraCT Number: 2019-003781-41 Sponsor Protocol Number: CLTW888A11301 Start Date*: 2026-11-02
    Sponsor Name:Novartis Pharma K.K
    Full Title: An open-label, single-arm study to provide efficacy and safety data of voretigene neparvovec administered assubretinal injection in Japanese patients with biallelic RPE65 mutation-associated retina...
    Medical condition: Biallelic RPE65 mutation-associated retinal dystrophy
    Disease: Version SOC Term Classification Code Term Level
    20.0 10015919 - Eye disorders 10038857 Retinal dystrophy PT
    Population Age: Children, Adolescents, Under 18, Adults Gender: Male, Female
    Trial protocol: Outside EU/EEA
    Trial results: (No results available)
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    The status and protocol content of GB trials is no longer updated since 1 January 2021. For the UK, as of 31 January 2021, EU Law applies only to the territory of Northern Ireland (NI) to the extent foreseen in the Protocol on Ireland/NI. Legal notice
    As of 31 January 2023, all EU/EEA initial clinical trial applications must be submitted through CTIS . Updated EudraCT trials information and information on PIP/Art 46 trials conducted exclusively in third countries continues to be submitted through EudraCT and published on this website.

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