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Clinical trials for Lesch-Nyhan syndrome

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    The EU Clinical Trials Register currently displays   44364   clinical trials with a EudraCT protocol, of which   7388   are clinical trials conducted with subjects less than 18 years old.   The register also displays information on   18700   older paediatric trials (in scope of Article 45 of the Paediatric Regulation (EC) No 1901/2006).

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    2 result(s) found for: Lesch-Nyhan syndrome. Displaying page 1 of 1.
    EudraCT Number: 2012-002662-12 Sponsor Protocol Number: PSY102 Start Date*: 2012-12-12
    Sponsor Name:Psyadon Pharmaceuticals Inc.
    Full Title: An Outpatient Phase 3 Efficacy Study of Ecopipam (PSYRX 101) in the Symptomatic Treatment of Self-Injurious Behavior in Subjects with Lesch-Nyhan Disease (LND).
    Medical condition: Self-injurious behavior in subjects with Lesch-Nyhan Disease (LND).
    Disease: Version SOC Term Classification Code Term Level
    15.0 10010331 - Congenital, familial and genetic disorders 10024245 Lesch-Nyhan syndrome LLT
    Population Age: Children, Adolescents, Under 18, Adults Gender: Male, Female
    Trial protocol: ES (Ongoing) NL (Prematurely Ended)
    Trial results: (No results available)
    EudraCT Number: 2007-004036-23 Sponsor Protocol Number: BIRD-LNS-07/07 Start Date*: 2008-06-23
    Sponsor Name:FONDAZIONE MALATTIE RARE MAURO BASCHIROTTO B.I.R.D. ONLUS
    Full Title: Efficacy and safety of S-adenosil-methionine on depression of patients with Lesch - Nyhan Syndrome
    Medical condition: Depressionin patients affected by Lesch - Nyhan disease
    Disease: Version SOC Term Classification Code Term Level
    6.1 10052636 HLT
    Population Age: Adults Gender: Male
    Trial protocol: IT (Completed)
    Trial results: (No results available)
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    The status and protocol content of GB trials is no longer updated since 1 January 2021. For the UK, as of 31 January 2021, EU Law applies only to the territory of Northern Ireland (NI) to the extent foreseen in the Protocol on Ireland/NI. Legal notice
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