- Trials with a EudraCT protocol (12)
- Paediatric studies in scope of Art45 of the Paediatric Regulation (0)
12 result(s) found for: Adrenoleukodystrophy.
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EudraCT Number: 2015-002805-13 | Sponsor Protocol Number: LTF-304 | Start Date*: 2015-11-27 | |||||||||||
Sponsor Name:bluebird bio, Inc | |||||||||||||
Full Title: Longterm Follow-up of Subjects With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product | |||||||||||||
Medical condition: Cerebral Adrenoleukodystrophy (CALD) | |||||||||||||
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Population Age: Children, Adolescents, Under 18 | Gender: Male | ||||||||||||
Trial protocol: GB (GB - no longer in EU/EEA) FR (Ongoing) NL (Ongoing) IT (Ongoing) | |||||||||||||
Trial results: (No results available) |
EudraCT Number: 2011-001953-10 | Sponsor Protocol Number: ALD-102 | Start Date*: 2013-12-13 | |||||||||||
Sponsor Name:bluebird bio, Inc. | |||||||||||||
Full Title: A phase 2/3 study of the efficacy and safety of hematopoietic stem cells transduced with Lenti D lentiviral vector for the treatment of cerebral adrenoleukodystrophy (CALD) | |||||||||||||
Medical condition: Cerebral Adrenoleukodystrophy (CALD) | |||||||||||||
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Population Age: Children, Adolescents, Under 18 | Gender: Male | ||||||||||||
Trial protocol: GB (GB - no longer in EU/EEA) FR (Completed) DE (Completed) Outside EU/EEA | |||||||||||||
Trial results: View results |
EudraCT Number: 2018-001145-14 | Sponsor Protocol Number: ALD-104 | Start Date*: 2019-04-17 | |||||||||||
Sponsor Name:bluebird bio, Inc. | |||||||||||||
Full Title: A Phase 3 Study of Lenti-D Drug Product After Myeloablative Conditioning Using Busulfan and Fludarabine in Subjects ≤17 Years of Age With Cerebral Adrenoleukodystrophy (CALD) | |||||||||||||
Medical condition: Cerebral Adrenoleukodystrophy (CALD) | |||||||||||||
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Population Age: Children, Adolescents, Under 18 | Gender: Male | ||||||||||||
Trial protocol: GB (GB - no longer in EU/EEA) FR (Ongoing) DE (Completed) NL (Completed) IT (Completed) | |||||||||||||
Trial results: View results |
EudraCT Number: 2019-000654-59 | Sponsor Protocol Number: MT-2-02 | Start Date*: 2019-06-25 | |||||||||||
Sponsor Name:Minoryx Therapeutics S.L. | |||||||||||||
Full Title: An exploratory, open-label, multicenter study in male pediatric patients with cerebral X-linked Adrenoleukodystrophie (cALD) to assess the effect of MIN-102 treatment on the progression of cerebral... | |||||||||||||
Medical condition: Cerebral X-linked Adrenoleukodystrophy (cALD) | |||||||||||||
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Population Age: Children, Adolescents, Under 18 | Gender: Male | ||||||||||||
Trial protocol: ES (Ongoing) DE (Ongoing) FR (Ongoing) | |||||||||||||
Trial results: (No results available) |
EudraCT Number: 2010-024084-40 | Sponsor Protocol Number: XAMNANTIOXAP2010 | Start Date*: 2011-06-30 | |||||||||||
Sponsor Name:Aurora Pujol Onofre | |||||||||||||
Full Title: Ensayo clínico en adrenomieloneuropatía (AMN): validación de biomarcadores de estrés oxidativo, eficacia y tolerancia de la combinación de antioxidantes N-acetilcisteína, ácido lipoico y vitamina E | |||||||||||||
Medical condition: Adrenoleucodistrofia ligada al X (XALD), fenotipo Adrenomieloneuropatía (AMN). | |||||||||||||
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Population Age: Adults, Elderly | Gender: Male, Female | ||||||||||||
Trial protocol: ES (Prematurely Ended) | |||||||||||||
Trial results: View results |
EudraCT Number: 2017-001684-21 | Sponsor Protocol Number: NV1205-009 | Start Date*: 2018-04-20 |
Sponsor Name:Neurov Acquisition LLC | ||
Full Title: Phase I/II, Open-Label, Dose Escalation Study of the Safety, Pharmacokinetics, and Pharmacodynamics of NV1205 in Pediatric Male Subjects with Childhood Cerebral Adrenoleukodystrophy (CCALD) | ||
Medical condition: Childhood Cerebral Adrenoleukodystrophy (CCALD) | ||
Disease: | ||
Population Age: Children, Adolescents, Under 18 | Gender: Male | |
Trial protocol: GB (Prematurely Ended) FR (Ongoing) | ||
Trial results: View results |
EudraCT Number: 2017-000748-16 | Sponsor Protocol Number: MT-2-01 | Start Date*: 2017-09-14 |
Sponsor Name:Minoryx Therapeutics S.L. | ||
Full Title: A RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED, MULTINATIONAL, MULTICENTER STUDY WITH OPEN-LABEL TREATMENT EXTENSION TO ASSESS THE EFFECT OF MIN-102 ON THE PROGRESSION OF ADRENOMYELONEUROPATHY IN M... | ||
Medical condition: ADRENOMYELONEUROPATHY IN MALE PATIENTS WITH X-LINKED ADRENOLEUKODYSTROPHY | ||
Disease: | ||
Population Age: Adults | Gender: Male | |
Trial protocol: GB (GB - no longer in EU/EEA) DE (Ongoing) HU (Ongoing) ES (Ongoing) NL (Ongoing) PL (Prematurely Ended) IT (Ongoing) | ||
Trial results: (No results available) |
EudraCT Number: 2011-006113-34 | Sponsor Protocol Number: XAMNPIOAP2011 | Start Date*: 2013-10-24 |
Sponsor Name:AURORA PUJOL ONOFRE | ||
Full Title: Effect of pioglitazone administred to patients with Adrenomyeloneuropathy: A phase II, Singlearm, Monocentric Trial. | ||
Medical condition: X-linked adrenoleukodystrophy | ||
Disease: | ||
Population Age: Adults | Gender: Male, Female | |
Trial protocol: ES (Ongoing) | ||
Trial results: (No results available) |
EudraCT Number: 2004-000592-33 | Sponsor Protocol Number: N/A | Start Date*: 2006-03-02 | ||||||||||||||||
Sponsor Name:Gentium S.p.A [...] | ||||||||||||||||||
Full Title: Prospective Study of the Incidence and Outcome of Venoocclusive Disease (VOD) with the Prophylactic Use of Defibrotide (DF, Gentium, Italy) in Pediatric Stem Cell Transplantation | ||||||||||||||||||
Medical condition: Hepatic veno-occlusive disease following hematopoietic stem cell transplantation | ||||||||||||||||||
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Population Age: Newborns, Infants and toddlers, Children, Adolescents, Under 18 | Gender: Male, Female | |||||||||||||||||
Trial protocol: SE (Completed) IE (Completed) GB (Completed) AT (Completed) IT (Completed) CZ (Completed) | ||||||||||||||||||
Trial results: (No results available) |
EudraCT Number: 2009-017026-39 | Sponsor Protocol Number: UCBT-002 | Start Date*: 2009-12-28 | |||||||||||
Sponsor Name:Aldagen, Inc | |||||||||||||
Full Title: A PHASE III TRIAL OF ALD-101 ADUVANT THERAPY of UNRELATED UMBILICAL CORD BLOOD TRANSPLANTATION (UCBT) IN PATIENTS WITH INBORN ERRORS OF METABOLISM | |||||||||||||
Medical condition: Inborn errors of metabolism | |||||||||||||
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Population Age: Newborns, Infants and toddlers, Children, Adolescents, Under 18 | Gender: Male, Female | ||||||||||||
Trial protocol: NL (Ongoing) | |||||||||||||
Trial results: (No results available) |
EudraCT Number: 2009-011921-15 | Sponsor Protocol Number: UCBT-002 | Start Date*: 2009-06-22 | |||||||||||
Sponsor Name:Aldagen, Inc | |||||||||||||
Full Title: A PHASE III TRIAL OF ALD-101 ADUVANT THERAPY of UNRELATED UMBILICAL CORD BLOOD TRANSPLANTATION (UCBT) IN PATIENTS WITH INBORN ERRORS OF METABOLISM | |||||||||||||
Medical condition: Inborn errors of metabolism | |||||||||||||
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Population Age: Newborns, Infants and toddlers, Children, Adolescents, Under 18 | Gender: Male, Female | ||||||||||||
Trial protocol: NL (Not Authorised) | |||||||||||||
Trial results: (No results available) |
EudraCT Number: 2011-004730-34 | Sponsor Protocol Number: 361.11 | Start Date*: 2011-07-20 | |||||||||||
Sponsor Name:OSPEDALE PEDIATRICO BAMBINO GESU' DI ROMA | |||||||||||||
Full Title: A phase II multicentre, randomized, controlled open-label study on the use of anti-thymocyte globulin and rituximab for immunomodulation of graft-versus-host disease in allogeneic matched transpla... | |||||||||||||
Medical condition: graft-versus-host disease | |||||||||||||
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Population Age: Infants and toddlers, Children, Adolescents, Under 18, Adults | Gender: Male, Female | ||||||||||||
Trial protocol: IT (Ongoing) | |||||||||||||
Trial results: (No results available) |
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